Enzyme Replacement Therapy

Hipofosfatasia: nuevas perspectivas terapéuticas

Genetics of complex disease / Humans / Inborn errors of metabolism / Parathyroid Hormone / Alkaline phosphatase / Medicina Clinica / Enzyme Replacement Therapy / Medicina Clinica / Enzyme Replacement Therapy

Fabry disease: a review

Family history / Heart Failure / Humans / Hemodialysis / Visual Impairment / Enzyme / Fabry Disease / Clinical Sciences / Chronic Renal Failure / Kidney Transplant / Enzyme Replacement Therapy / Enzyme / Fabry Disease / Clinical Sciences / Chronic Renal Failure / Kidney Transplant / Enzyme Replacement Therapy

Anti-α-galactosidase A antibody response to agalsidase beta treatment: Data from the Fabry Registry

Treatment Outcome / Humans / Female / Male / Fabry Disease / Clinical Sciences / Isoenzymes / Alpha-Galactosidase / Enzyme Replacement Therapy / immunoglobulin G / Clinical Sciences / Isoenzymes / Alpha-Galactosidase / Enzyme Replacement Therapy / immunoglobulin G
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