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Enzyme Replacement Therapy
Enzyme Replacement Therapy
Hipofosfatasia: nuevas perspectivas terapéuticas
Genetics of complex disease / Humans / Inborn errors of metabolism / Parathyroid Hormone / Alkaline phosphatase / Medicina Clinica / Enzyme Replacement Therapy / Medicina Clinica / Enzyme Replacement Therapy
Fabry disease: a review
Family history / Heart Failure / Humans / Hemodialysis / Visual Impairment / Enzyme / Fabry Disease / Clinical Sciences / Chronic Renal Failure / Kidney Transplant / Enzyme Replacement Therapy / Enzyme / Fabry Disease / Clinical Sciences / Chronic Renal Failure / Kidney Transplant / Enzyme Replacement Therapy
Anti-α-galactosidase A antibody response to agalsidase beta treatment: Data from the Fabry Registry
Treatment Outcome / Humans / Female / Male / Fabry Disease / Clinical Sciences / Isoenzymes / Alpha-Galactosidase / Enzyme Replacement Therapy / immunoglobulin G / Clinical Sciences / Isoenzymes / Alpha-Galactosidase / Enzyme Replacement Therapy / immunoglobulin G
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